Wednesday, 15 August 2018
News with tag Gene therapy  RSS
Amish nemaline myopathy natural history study finds promise for gene therapy treatment

Added: 13.08.2018 19:27 | 10 views | 0 comments

A new comprehensive natural history study about Amish nemaline myopathy (ANM) in the Old Order Amish population focuses on the promise of gene therapy for this lethal disorder. Amish nemaline myopathy (ANM) is an infantile-onset muscle disease linked to a mutation of the TNNT1 gene. The study summarizes genealogical records, clinical data, and molecular reports of one hundred and six ANM patients born between 1923 and 2017.

From: https:

They Thought Hemophilia Was a ‘Lifelong Thing.’ They May Be Wrong.

Added: 13.08.2018 15:35 | 16 views | 0 comments

Experimental gene therapies have yielded promising results in early trials. But the drugs have left some patients wary, worried that success will not last.

From: https:

Gene therapy shown to cure type 2 diabetes and obesity in mice, researchers report

Added: 09.08.2018 17:52 | 5 views | 0 comments

A single administration of a therapeutic vector in mouse models cures type 2 diabetes and obesity in the absence of long-term side effects, researchers report. In healthy mice, the therapy prevents age-associated weight gain and insulin resistance and promotes healthy aging.

From: https:

Gene therapy with BMP4 protects against weight gain and insulin resistance in mice

Added: 29.08.2017 8:00 | 1 views | 0 comments

"By increasing BMP4, we can increase the metabolic rate, but we only see this in initially lean mice.


Biological bypass shows promise in coronary artery disease

Added: 11.08.2017 8:00 | 0 views | 0 comments

A new gene therapy that targets the heart and requires only one treatment session has been found safe for patients with coronary artery disease, according to a successful trial carried out in Finland.



Copyright © 2008-2018 USweekly  - all rights reserved