A new gene therapy that targets the heart and requires only one treatment session has been found safe for patients with coronary artery disease, according to a successful trial carried out in Finland.

Scientist have now overcome challenges that have limited the use of gene therapy. They demonstrate how their novel approach with skin transplantation could enable a wide range of gene-based therapies to treat human diseases. The researchers provide 'proof-of-concept,' treating mice with two common related human ailments: type-2 diabetes and obesity.

Gene therapy for cancer is becoming a reality but works best for blood cancers like leukemia and not so well yet in more common ones like lung cancer.

Scientists investigating the genetic causes and altered functioning of nerve cells in motor neurone disease (MND) have discovered a new mechanism that could lead to fresh treatment approaches for one of the most common forms of the disease.

July 14, 2017 5:00 AM
NEW YORK • A Food and Drug Administration (FDA) panel has opened a new era in medicine by unanimously recommending that the agency approve the first treatment that genetically alters a patient's own cells to fight cancer.

A novel airway-delivered gene therapy for treating pulmonary hypertension (PH), a form of high blood pressure in blood vessels in the lungs that is linked to heart failure, has been advanced by new research.